A study, conducted in several sites, with a duration of 2 years to evaluate the Safety and Efficacy of a new drug named velmanase alfa used in children with Alpha-Mannosidosis below 6 years of age

Update Il y a 4 ans
Reference: EUCTR2016-001988-36

Woman and Man

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Extract

The main objectives of this trial are to evaluate safety and efficacy of repeated velmanase alfa i.v. infusions in pediatric alpha-mannosidosis patients aged less than 6 years" as per section 2 of the study protocol


Inclusion criteria

  • Alfa-mannosidosis

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